Study design and baseline characteristics for the reflect gene therapy trial ofm.11778g>A/ND4-LHON
Prem S Subramanian, Nancy J Newman, Mark Moster, An-Guor Wang, Patrick Yu-Wai-Man, Sean Donahue, Bart P Leroy, Valerio Carelli, Valerie Biousse, Catherine Vignal-Clermont, Robert C Sergott, Alfredo A Sadun, Gema Rebolleda, Bart K Chwalisz, Rudrani Banik, Fabienne Bazin, Eric Cox, Michel Roux, Magali Taiel, Jose-Alain Sahel
BMJ Open Ophthalmology Nov 2022, 7 (1) e001158; DOI: 10.1136/bmjophth-2022-001158